UMIN ID: UMIN000042015
Registered date:07/10/2020
Japan REgistry for Adult subjeCTs of SMA
Basic Information
| Recruitment status | Complete: follow-up continuing |
|---|---|
| Health condition(s) or Problem(s) studied | Spinal Muscular Atrophy |
| Date of first enrollment | 2020/11/01 |
| Target sample size | 150 |
| Countries of recruitment | Japan |
| Study type | Observational |
| Intervention(s) |
Outcome(s)
| Primary Outcome | Collecting longitudinal data of Motor function and QOL/PRO |
|---|---|
| Secondary Outcome |
Key inclusion & exclusion criteria
| Age minimum | 18years-old |
|---|---|
| Age maximum | Not applicable |
| Gender | Male and Female |
| Include criteria | |
| Exclude criteria | 1)SMA patients who have psychiatric disorder. 2)SMA patients who are judged as unsuitable for the study by the investigator. |
Related Information
| Primary Sponsor | Nagoya University Graduate School of Medicine Biogen Japan Ltd. Chugai Pharmaceutical Co., Ltd. |
|---|---|
| Secondary Sponsor | |
| Source(s) of Monetary Support | Biogen Japan Ltd. Chugai Pharmaceutical Co., Ltd. |
| Secondary ID(s) |
Contact
| public contact | |
| Name | Satona Otake |
| Address | Akasaka Intercity,1-11-44 Akasaka, Minato-ku,Tokyo, Japan Japan 107-0052 |
| Telephone | 03-4362-4500 |
| sma_adult_registry@mebix.co.jp | |
| Affiliation | Mebix, Inc. Research Promotion Group |
| scientific contact | |
| Name | Masahisa Katsuno |
| Address | 65 Tsurumai Showa, Nagoya, Aichi, Japan Japan |
| Telephone | 052-744-2389 |
| ka2no@med.nagoya-u.ac.jp | |
| Affiliation | Nagoya University Graduate School of Medicine Department of Neurology |