NIPH Clinical Trials Search

JAPANESE
国立保健医療科学院
JAPIC ID: JapicCTI-163291

Registered date:

Basic Information

Recruitment status
Health condition(s) or Problem(s) studiedDuchenne muscular dystrophy
Date of first enrollment01/4/2016
Target sample size16
Countries of recruitment
Study typeINTERVENTIONAL
Intervention(s)Intervention name : NS-065/NCNP-01 Dosage And administration of the intervention : intravenous infusion Control intervention name : null

Outcome(s)

Primary OutcomeEfficacy
Secondary OutcomeSafety, Pharmacokinetic profile

Key inclusion & exclusion criteria

Age minimum5
Age maximum17
GenderMale
Include criteria1) Ambulant or non-ambulant patient 2) Able to treat with skipping of exon 53
Exclude criteriaHas participated in other clinical trial that might recover dystrophin protein by the readthrough or the exon-skipping therapy, and/or upregulate the dystrophin-associated proteins such as utrophin.

Related Information

Contact

public contact
Name NIPPON SHINYAKU CO., LTD. Corporate Communications Dept.
Address kouhou@mb.nippon-shinyaku.co.jp
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scientific contact
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